Effectiveness and tolerability of migalastat in adult Fabry disease: A single regional centre experience.

Galafold (migalastat) - BioMarin

http://www.ncbi.nlm.nih.gov/pubmed/42181773

Ana Jovanovic; Eamon P McCarron; John Bassett; Jonathan Meyer; Karolina M Stepien; Peter Woolfson; Rajkumar Chinnadurai; Reena Sharma

May 26, 2026