miglustat - Generic mfg.
Pombiliti (cipaglucosidase alfa-atga) - Amicus
https://www.aan.com/msa/Public/Events/AbstractDetails/61853
 
Alberto di Ronza1; Drago Bratkovic2; Barry J. Byrne3; Paula R. Clemens4; Ozlem Goker-Alpan5; Priya S. Kishnani6; Tahseen Mozaffar7; Mark Roberts8; Nadine AME Van Der Beek9; Farah Amon1; Brian Fox1; Fred Holdbrook1; Vipul Jain1; Benedikt Schoser10
 
Mar 6, 2026
 
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