Galafold (migalastat) - BioMarin
https://onlinelibrary.wiley.com/doi/epdf/10.1002/jimd.70230
 
Ida Vanessa Doederlein Schwartz 1,5,4; Ana Paula Pedroso Junges 1,2,5; Luciana Gaudenzi Heuser 5,5; César Augusto dos Santos Vieira 5,6; Bruna Bento dos Santos 5; Alicia Dornelles Dorneles 1,5,4
 
Aug 17, 2026
 
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