Cipaglucosidase alfa plus miglustat in Pompe disease: two non-ambulatory patients switching from high‑dose, high-frequency alglucosidase alfa.

miglustat - Generic mfg.

Pombiliti (cipaglucosidase alfa-atga) - Amicus

Myozyme (alglucosidase alfa) - Sanofi

http://www.ncbi.nlm.nih.gov/pubmed/41270519

Barry J Byrne; Jeff Castelli; Jennifer Zhang; Sheela Sitaraman Das; Vipul Jain

Nov 22, 2025