Galafold (migalastat) - Amicus
Elfabrio (pegunigalsidase alfa-iwxj) - Protalix, Chiesi
Fabrazyme (agalsidase beta) - Sanofi
Replagal (agalsidase alfa) - Samaritan Pharma, Takeda
https://www.ispor.org/conferences-education/conferences/upcoming-conferences/ispor-europe-2025/program/program/paper/ispor-europe-2025/poster-session-1-2/what-has-worked-well-in-fabry-disease-an-hta-landscape-assessment-study
 
Raju Gautam, PhD 1; Ratna Pandey, MSc 2; Shilpi Swami, MSc 1; Tushar Srivastava, MSc 1.
 
Nov 11, 2025
 
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