Cipaglucosidase alfa and miglustat for treatment of late-onset Pompe disease (LOPD): A therapeutics bulletin of the American College of Medical Genetics and Genomics (ACMG).

Pombiliti (cipaglucosidase alfa-atga) - Amicus

http://www.ncbi.nlm.nih.gov/pubmed/40893835

; Allyson Derry; Elizabeth K Baker; Irene J Chang; Jennifer L Cohen

Sep 4, 2025