Galafold (migalastat) - Amicus
Elfabrio (pegunigalsidase alfa-iwxj) - Protalix, Chiesi
Fabrazyme (agalsidase beta) - Sanofi
Replagal (agalsidase alfa) - Samaritan Pharma, Takeda
http://www.ncbi.nlm.nih.gov/pubmed/40310476
 
Elise Raphaela Menke; Eva Brand; Malte Lenders
 
May 1, 2025
 
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