Galafold (migalastat) - Amicus
lucerastat (ACT-434964) - Idorsia
venglustat (GZ402671) - Sanofi
Elfabrio (pegunigalsidase alfa-iwxj) - Protalix, Chiesi
Replagal (agalsidase alfa) - Samaritan Pharma, Takeda
http://www.ncbi.nlm.nih.gov/pubmed/40288367
 
Fernando Perretta; Gustavo Cabrera; Juan Politei
 
Apr 28, 2025
 
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