RNA Exon Editing for Stargardt Disease: Non-clinical Development and First-in-Human Clinical Safety of ACDN-01

ACDN-01 - Ascidian Therap

https://pag.virtual-meeting.org/US/asgct2026/en-US/pag/presentation/684765

Murray Abramson1; Alia Rashid1; John Bachmann1; Kirk Burkhart1; Ting-Wen Cheng1; Tayla Cormier1; Akiko Doi1; John Kerwin1; Xiaojin Liu1; Sangeetha Manokaran1; Lai Mung Fong1; Akiko Noma1; Anika Pavis1; Michael Ehlers1; Robert Bell1

Mar 22, 2026