CRISPR_SCD001
/ University of California
- LARVOL DELTA
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September 20, 2024
Transplantation of Clustered Regularly Interspaced Short Palindromic Repeats Modified Hematopoietic Progenitor Stem Cells (CRISPR_SCD001) in Patients with Severe Sickle Cell Disease
(clinicaltrials.gov)
- P1/2 | N=9 | Not yet recruiting | Sponsor: Mark Walters, MD | Trial completion date: Jun 2028 ➔ Mar 2029 | Trial primary completion date: Jun 2025 ➔ Mar 2027 | Not yet recruiting ➔ Recruiting
Enrollment open • Trial completion date • Trial primary completion date • Genetic Disorders • Hematological Disorders • Sickle Cell Disease • Transplantation
January 09, 2023
Transplantation of Clustered Regularly Interspaced Short Palindromic Repeats Modified Hematopoietic Progenitor Stem Cells (CRISPR_SCD001) in Patients With Severe Sickle Cell Disease
(clinicaltrials.gov)
- P1/2 | N=9 | Not yet recruiting | Sponsor: Mark Walters, MD | Trial completion date: Dec 2027 ➔ Jun 2028 | Trial primary completion date: Dec 2024 ➔ Jun 2025
Trial completion date • Trial primary completion date • Genetic Disorders • Hematological Disorders • Sickle Cell Disease • Transplantation • HP
April 27, 2022
Transplantation of Clustered Regularly Interspaced Short Palindromic Repeats Modified Hematopoietic Progenitor Stem Cells (CRISPR_SCD001) in Patients With Severe Sickle Cell Disease
(clinicaltrials.gov)
- P1/2 | N=9 | Not yet recruiting | Sponsor: Mark Walters, MD | Trial completion date: Dec 2026 ➔ Dec 2027 | Trial primary completion date: Dec 2023 ➔ Dec 2024
Trial completion date • Trial primary completion date • Genetic Disorders • Hematological Disorders • Sickle Cell Disease • Transplantation • HP
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