vesemnogene lantuparvovec (AAV-hSMN1)
/ Lantu Biopharma
- LARVOL DELTA
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December 05, 2025
Real World Clinical Effectiveness & Safety of Vesemnogene Lantuparvovec for Spinal Muscular Atrophy (SMA) in Low-middle Income Countries (LMIC).
(clinicaltrials.gov)
- P3 | N=15 | Recruiting | Sponsor: Lantu Biopharma
New P3 trial • Real-world evidence • Genetic Disorders • Movement Disorders • Muscular Atrophy • Rare Diseases
October 09, 2024
An Open Label Study of Gene Therapy Product (Vesemnogene Lantuparvovec) in Spinal Muscular Atrophy
(clinicaltrials.gov)
- P1/2 | N=6 | Recruiting | Sponsor: Lantu Biopharma | Trial completion date: Jul 2027 ➔ Oct 2027 | Trial primary completion date: Jul 2027 ➔ Oct 2027
Gene therapy • Trial completion date • Trial primary completion date • Gene Therapies • Genetic Disorders • Movement Disorders • Muscular Atrophy • Rare Diseases
July 19, 2024
An Open Label Study of Gene Therapy Product (Vesemnogene Lantuparvovec) in Spinal Muscular Atrophy
(clinicaltrials.gov)
- P1/2 | N=6 | Recruiting | Sponsor: Lantu Biopharma | Not yet recruiting ➔ Recruiting | Trial completion date: Mar 2027 ➔ Jul 2027 | Initiation date: Mar 2024 ➔ Jul 2024 | Trial primary completion date: Mar 2027 ➔ Jul 2027
Enrollment open • Gene therapy • Trial completion date • Trial initiation date • Trial primary completion date • Gene Therapies • Genetic Disorders • Movement Disorders • Muscular Atrophy • Rare Diseases
March 01, 2024
An Open Label Study of Gene Therapy Product in Spinal Muscular Atrophy Patients
(clinicaltrials.gov)
- P1/2 | N=6 | Not yet recruiting | Sponsor: Lantu Biopharma
New P1/2 trial • Gene Therapies • Genetic Disorders • Movement Disorders • Muscular Atrophy • Rare Diseases
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