AAVrh.10CUhCLN2 / Cornell University, National Institutes of Health - LARVOL DELTA

Safety Study of a Gene Transfer Vector (Rh.10) for Children With Late Infantile Neuronal Ceroid Lipofuscinosis (LINCL) (clinicaltrials.gov) - P1; N=12; Completed; Sponsor: Weill Medical College of Cornell University; Active, not recruiting ➔ Completed; N=25 ➔ 12; Trial completion date: Aug 2032 ➔ Dec 2020

Clinical • Enrollment change • Trial completion • Trial completion date • CNS Disorders • Gene Therapies • MRI