Tegsedi (inotersen) - Ionis, SOBI
Attruby (acoramidis) - BridgeBio
Wainua (eplontersen) - Ionis, AstraZeneca
Onpattro (patisiran) - Alnylam, Sanofi
Vyndaqel (tafamidis meglumine) - Pfizer
nexiguran ziclumeran (NTLA-2001) - Intellia Therap, Regeneron
Amvuttra (vutrisiran) - Alnylam
http://www.ncbi.nlm.nih.gov/pubmed/42458194
 
Haruki Koike; Masaaki Yoshikawa; Toshihiro Ide
 
Jul 16, 2026
 
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