Attruby (acoramidis) - BridgeBio
Wainua (eplontersen) - Ionis, AstraZeneca
Onpattro (patisiran) - Alnylam, Sanofi
Vyndaqel (tafamidis meglumine) - Pfizer
Amvuttra (vutrisiran) - Alnylam
http://www.ncbi.nlm.nih.gov/pubmed/42423415
 
Bo-Göran Ericzon; Giampaolo Merlini; João Beirão; John L Berk; Jonas Wixner; Laura Obici; Luísa Lobato; Márcia Waddington Cruz; Marianna Fontana; Markus Weiler; Mathew S Maurer; Mitsuharu Ueda; Pablo Garcia-Pavia; Ronald M Witteles; Teresa Coelho; Violaine Planté-Bordeneuve; Yoshiki Sekijima; Yukio Ando
 
Jul 10, 2026
 
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