Nexviazyme (avalglucosidase alfa) - Sanofi
miglustat - Generic mfg.
Vimizim (elosulfase alfa) - BioMarin
Aldurazyme (laronidase) - BioMarin, Sanofi
Naglazyme (galsulfase) - AnGes MG, BioMarin
Fabrazyme (agalsidase beta) - Sanofi
Myozyme (alglucosidase alfa) - Sanofi
https://onlinelibrary.wiley.com/doi/epdf/10.1002/jimd.70230
 
Antonio Ochoa-Ferraro 1; Zoe Taylor 2; Faiza Adrees 5; Daniel Bell 4; Susan McMahn 5; Evelyn Frank 6; Chin Gan 7; Siema Akram 8; Niamh Finnegan 9; Robert Dugdale 10; Clara Monaghan 11; Thomas Wyllie 12
 
Aug 17, 2026
 
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