Improved outcome with early introduction of ERT in MPS VI: a sibling study in Brazil

Naglazyme (galsulfase) - AnGes MG, BioMarin

https://onlinelibrary.wiley.com/doi/epdf/10.1002/jimd.70230

Ana Cecilia Menezes de Siqueira 1; Luis Felipe Siqueira Ribeiro 1; Gabrielle Paraiso Cabral de Oliveira 1; Rosangela Maria Lima Santos 1; Kristiane Michelin-Tirelli 2; Franciele Trapp 5; Mariluce Riegel 5; Roberto Giugliani 2,5,4,5

Aug 17, 2026