Galafold (migalastat) - Amicus
venglustat (GZ402671) - Sanofi
Fabrazyme (agalsidase beta) - Sanofi
Replagal (agalsidase alfa) - Samaritan Pharma, Takeda
http://clinicaltrials.gov/ct2/show/NCT05280548
 
Dec 18, 2024
 
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