Pharmacokinetic evaluation of single-dose migalastat in non-Fabry disease subjects with ESRD receiving dialysis treatment, and use of modeling to select dose regimens in Fabry disease subjects with ESRD receiving dialysis treatment.

Galafold (migalastat) - Amicus

http://www.ncbi.nlm.nih.gov/pubmed/39636942

Anthony Sileno; Atef Halabi; Franklin K Johnson; Ginny Schmith; Hadis Williams; Jasmine Rutecki; Shirley Wu; Thorsten Feldkamp

Dec 5, 2024