miglustat - Generic mfg.
Pombiliti (cipaglucosidase alfa-atga) - Amicus
https://acmg.planion.com/Web.User/AbstractDet?ACCOUNT=ACMG&ABSID=868974&CONF=AM26&ssoOverride=OFF&CKEY=O4O0G3O53
 
Priya S. Kishnani; Drago Bratkovic, MD MBBS FRACP; Barry J. Byrne, MD PhD; Paula R. Clemens, MD; Ozlem Goker-Alpan, MD; Tahseen Mozaffar, MD; Mark Roberts, MD, PhD; Nadine van der Beek, MD; Farah Amon, MS, PMP; Brian Fox, PhD; Fred Holdbrook, PhD; Vipul Jain, MS MBA; Benedikt Schoser, MD, PhD
 
Jan 17, 2026
 
Prev Next