Pombiliti (cipaglucosidase alfa-atga) - Amicus
Myozyme (alglucosidase alfa) - Sanofi
https://acmg.planion.com/Web.User/AbstractDet?ACCOUNT=ACMG&ABSID=869737&CONF=AM26&ssoOverride=OFF&CKEY=O4O0G3O53
 
Priya S. Kishnani; Drago Bratkovic, MD MBBS FRACP; Kristl G. Claeys, MD, PhD; Jordi Díaz-Manera, MD, Prof; Michael I. Polkey, FRCP, PhD; Mark Roberts, MD, PhD; Benedikt Schoser, MD, PhD; Antonio Toscano, MD, Prof; Fred Holdbrook, PhD; Vipul Jain, MS MBA; Pilar Moore, AD; Kinesha O'Brien-Prince, MPH; Tahseen Mozaffar, MD
 
Jan 17, 2026
 
Prev Next